CIBMTR Center Number: CIBMTR Recipient ID: RETIRED. EBMT Center Identification Code (CIC): Today s Date:

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Multiple Sclerosis Pre-HSCT Data EBMT Center Identification Code (CIC): Today s Date: Sequence Number: Date Received: Registry Use Only Date of HSCT for which this form is being completed: & 20 20 HSCT type: o autologous o allogeneic, o allogeneic, o syngeneic unrelated related (identical twin) Product type: o marrow o PBSC o cord blood o other product, specify: This form must be accompanied by Form 2000 Recipient Baseline Data. All information in the box above, including the date, should be identical with the corresponding Form 2000. Information should come from an actual examination by the Transplant Center physician, or the physician who is following the recipient pre-hsct, or abstraction of the recipient s medical records. Questions followed by the book symbol & indicate additional information necessary to complete the question is referenced in the forms instruction manual. If this is a report of a second or subsequent transplant, check here o and continue with question 42. Disease Assessment at Diagnosis 1. What was the date of onset for the first Multiple Sclerosis (MS) symptom(s)? o date unknown 2. What was the date of diagnosis of MS? o date unknown 3. Are any of the recipient s family members also affected with MS? Specify the family members: 4. Monozygotic twin 5. Dizygotic twin 6. Other first degree relative (sibling, parent, child) 7. Second degree relative (grandparent, aunt, uncle, first cousin) 8. Other relative 9. Specify relationship: Laboratory Studies at Diagnosis Specify results of tests performed prior to any first treatment given for MS. 10. Was the diagnosis of MS corroborated by laboratory or radiological test results? Specify which test measures indicated MS: 11. CSF oligoclonal bands present 12. Elevated IgG index 13. MRI brain lesions consistent with MS CIBMTR Form 2043 revision 2 (page 1 of 5) March 2011 Mail this form to your designated campus (Milwaukee or Minneapolis). Retain the original at the transplant center.

Pre-HSCT Treatment for Multiple Sclerosis 14. Did the recipient receive any disease-modifying treatments between the time of diagnosis and prior to mobilization for stem cell collection (or prior to the preparative regimen if mobilization was not done)? Continue with table below Continue with question 42 15. Specify the date the first disease-modifying therapy started: Indicate all treatments for MS that the recipient received prior to mobilization for stem cell collection (or prior to the preparative regimen if mobilization was not done): 16. Alemtuzumab (Campath) 17. Azathioprine (Azasan, Imuran) 18. Belimumab (LymphoStat-B) 19. Cladribine (2-CdA, Leustatin) 20. Corticosteroids & (chronic use, not to treat acute relapse) 21. Cyclophosphamide (CTX, Cytoxan, Neosar) 22. Daclizumab (Zenapax, anti-cd25) 23. Fingolimod (FTY720) 24. Fumarate (oral) (BG00012) 25. Glatiramer acetate (Copaxone) [previously copolymer-1] 26. Immune globulin (IVIG, Gamimune, Gammagard) 27. Interferon beta-1a (Avonex, Rebif) 28. Interferon beta-1b (Betaseron) 29. Laquinimod 30. Methotrexate (MTX, Folex) 31. Mitoxantrone (Novantrone) 32. Natalizumab (Tysabri, Antegren) 33. Mycophenolate mofetil (MMF, Cellcept) 34. Rituximab (anti-cd20, Rituxan, MabThera) 35. Sirolimus (Rapamune) 36. Tacrolimus (FK 506, Prograf) 37. Teriflunomide (oral) (HMR1726) 38. Blinded randomized trial agent 39. Specify trial agent: 40. Other treatment 41. Specify other treatment: Baseline Assessment for MS Performed at the Transplant Center Information reported in this section should come from the recipient s first evaluation performed at the transplant center. For autologous HSCT recipients, the baseline assessment is typically 4 weeks prior to mobilization for stem cell collection. 42. Date of baseline evaluation: 43. Specify the number of relapses of MS during the 1-year period prior to the baseline assessment: o number unknown 44. Specify the disease course during the 2-year period prior to the baseline assessment: 1 o relapsing remitting 2 o secondary progressive 3 o primary progressive 4 o progressive relapsing 5 o unknown CIBMTR Form 2043 revision 2 (page 2 of 5) March 2011

45. Was the Kurtzke Expanded Disability Status Scale (EDSS) assessed by a neurologist during the 2-year period prior to the baseline assessment? 46. Date of EDSS assessment: 47. EDSS: 48. Date of EDSS assessment: 49. EDSS: 50. Date of EDSS assessment: 51. EDSS: 52. Date of EDSS assessment: 53. EDSS: 54. Date of EDSS assessment: 55. EDSS: 56. Were the Kurtzke Functional Systems Scores (FSS) assessed by a neurologist during the baseline assessment? Specify the following FSS scores: 57. Pyramidal: o score unknown 58. Cerebellar: o score unknown 59. Brainstem: o score unknown 60. Sensory: o score unknown 61. Bowel and bladder: o score unknown 62. Visual: o score unknown 63. Cerebral: o score unknown 64. Other function: 65. Specify other function: o score unknown 66. Specify the EDSS at baseline assessment: o EDSS unknown 67. Was a MRI scan of the brain conducted during the baseline assessment? 68. Date of baseline MRI: o date unknown 69. Are T2 lesions present on the MRI? 71. Was gadolinium contrast used for this assessment? 70. Specify number of T2 lesions: o number unknown 72. Are gadolinium-enhancing lesions present on the MRI? 73. Specify number o number of lesions: unknown CIBMTR Form 2043 revision 2 (page 3 of 5) March 2011

Stem Cell Mobilization for Autologous HSCT This section records pre-mobilization information for autologous HSCTs only; if this report is for an allogeneic HSCT, or if the autologous HSCT did not use mobilization, check here o and continue with question 79. 74. Did the recipient receive treatment, prior to any stem cell harvest, to enhance the autologous product collection for this HSCT? Specify treatment(s): (select all that apply) 75. Cyclophosphamide 76. Growth factors 77. Other mobilization chemotherapy Report details on form 2006 HSCT Infusion 78 Specify other chemotherapy: Most Recent Disease Assessment Prior to the Start of the Preparative (Conditioning) Regimen Information for this section should come from the most recent evaluation performed 2 weeks prior to the preparative regimen. If the recipient was not evaluated prior to the preparative regimen, check here o and continue with the signature lines at question 104. For recipients of autologous cells who underwent mobilization for stem cell collection, a second disease assessment is required prior to the preparative regimen. 79. Date of evaluation prior to the preparative regimen: 80. Specify the number of relapses of MS that occurred after the start of mobilization and the start of the preparative regimen: & o number unknown 81. Did the recipient experience worsening disability or continuous progression of MS between mobilization and the start of the preparative regimen? 82. Was a MRI scan of the brain conducted as part of the disease assessment prior to the preparative regimen (not including the baseline MRI reported at question 67)? 83. Date of most recent MRI performed prior to the preparative regimen: 84. Does the radiology report include a comparison with the baseline MRI? Continue with question 87 Complete questions 85 89, then continue at question 93. 85. Are T2 lesions present on the MRI? 86. Specify the number of T2 lesions: o number unknown 87. Was gadolinium contrast used for this assessment? 88. Are gadolinium-enhancing lesions present on the MRI? 89. Specify the number of 2 o o number no gadolinium-enhancing unknown lesions: CIBMTR Form 2043 revision 2 (page 4 of 5) March 2011

90. In comparison to the baseline MRI, does the radiology report state evidence of new or enlarged T2 lesions? 91. In comparison to the baseline MRI, does the radiology report state evidence of any new or enlarged gadolinium-enhancing lesions? 92. In comparison to the baseline MRI, does the radiology report a change in the overall burden of MS-specific lesions? 1 o improvement of lesion burden 2 o worsening of lesion burden 3 o mixed response 93. Were the Kurtzke Functional Systems Scores (FSS) assessed by a neurologist prior to the preparative regimen (not including any FSS reported at question 56)? Specify the following FSS scores: 94. Pyramidal: o score unknown 95. Cerebellar: o score unknown 96. Brainstem: o score unknown 97. Sensory: o score unknown 98. Bowel and bladder: o score unknown 99. Visual: o score unknown 100. Cerebral: o score unknown 101. Other function: 102. Specify other function: o score unknown 103. Specify the most recent EDSS assessed prior to the preparative regimen: o EDSS unknown If the person completing this form is a Neurologist, check here o and continue with the signautre lines below. 104. Signed: Please print name: Person completing form Phone: ( ) Fax: ( ) E-mail address: CIBMTR Form 2043 revision 2 (page 5 of 5) March 2011